What Challenges Do Families Face in Accessing Canavan Gene Therapy
When it comes to genetic diseases, Canavan disease stands as a significant obstacle for affected families. With recent advancements in medical science, gene therapy has emerged as an effective option.
But getting access to Canavan gene therapy is a difficult process that puts families into a complex web of emotional, financial, and logistical struggles.
Canavan disease is a rare genetic disorder that affects the central nervous system. It is defined by the degradation of white matter in the brain, which frequently results in a shorter lifespan, severe developmental delays, and intellectual disabilities.
Gene therapy is a modern medical strategy that attempts to treat the root cause of this genetic disease. The goal of the research is to replace the defective genetic mutations ...